Efficacy, Safety, and Durability of Gene Therapy for Inherited Retinal Diseases in the Pediatric Population: A Scoping Review.

چکیده

To map the published interventional gene-based therapies relevant to children with inherited retinal diseases (IRDs), with a focus on efficacy, safety, and durability, including pediatric-vs-adult patterns where available. This scoping review followed a prospectively registered protocol specifying…

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موضوعات مرتبط

• چشم پزشکی کودکان
• شبکیه