Real-world outcomes of Voretigene Neparvovec: a single-centre consecutive case series.

چکیده

To present functional and anatomical outcomes of subretinal therapy with Voretigene Neparvovec (VN) in patients treated in one of the four specialist UK gene therapy centres. Single-centre, retrospective case series of patients affected by an inherited retinal dystrophy (IRD) caused by a pathogenic…

متن کامل چکیده در سایت ناشر در دسترس است.

موضوعات مرتبط

• تصویربرداری و تشخیص