The efficacy and safety of adeno-associated virus-mediated gene therapy for CNGA3- and CNGB3-associated achromatopsia: A genotype-aware systematic review and meta-analysis.

چکیده

We evaluated the efficacy and safety of adeno-associated virus-mediated gene therapy for CNGA3 (Cyclic Nucleotide-Gated Channel Alpha 3)- and CNGB3 (Cyclic Nucleotide-Gated Channel Beta 3)-associated achromatopsia. Human studies were systematically searched from database inception to March, 2026,…

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